Neuromuscular Disorders 31 (2021) S47-S162with non-mandatory data items. Data collected through the dataset includes genetic diagnosis, clinical observations, scoliosis, motor function, ambulation, nutrition, pulmonary function, disease-modifying therapies, medication and rehabilitation, hospitalisations and comorbiditis. The dataset dictionary is publicly available and data harmonization has been undertaken with key stakeholders in the wider SMA community. One year on, this poster will present an updated overview on the progress of the Dataset implementation, collected through online surveys and virtual interviews with curators across the network. Additionally, we will present data from an enquiry into the TREAT-NMD global registry network for SMA, to demonstrate the impact of the expanded dataset and illustrate its potential use in PMS.

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